|New treatments provide hope for children with Spinal Muscular Atrophy|
Spinal Muscular Atrophy, or SMA, is a rare, debilitating and usually deadly disease that strikes children in infancy. But Dr. Lisa Baumbach-Reardon, a neurogenomics investigator at Phoenix's Translational Genomics Research Institute, or TGen, believes ...
azcentral.com - Thu, 28 Aug 2014 22:03
|Spinal Muscular Atrophy: Briley Faith's Story|
In March of this year I had the opportunity to write an article about Spinal Muscular Atrophy (SMA) entitled The Most Common Rare Genetic Disease You've Never Heard Of: SMA. The response from people was so positive that I wanted to write another ...
Parade - Thu, 21 Aug 2014 12:41
|Research Funding Connection between ALS and Spinal Muscular Atrophy from ...|
Families of Spinal Muscular Atrophy - Thu, 21 Aug 2014 07:37
|RNA Splicing Shows Positive Results in Spinal Muscular Atrophy Models|
An industry-university team reports that continuous treatment of mouse models of spinal muscular atrophy (SMA) with RNA splicing compounds increased life span, normalized body weight, and prevented both disease-related motor dysfunction and ...
Genetic Engineering & Biotechnology News - Fri, 08 Aug 2014 06:30
|Spinal Muscular Atrophy Mice Model Results Published in the Journal Science.|
Families of Spinal Muscular Atrophy - Thu, 07 Aug 2014 12:52
|Orally Delivered Compounds, Which Selectively Modify RNA Splicing Prevent ...|
MarketWatch - Thu, 07 Aug 2014 11:01
|Families of Spinal Muscular Atrophy Provides Thousands of SMA Families ...|
Along with funding SMA research, Families of Spinal Muscular Atrophy provides thousands of families with vital family support and resources that help families navigate life with SMA. Families of SMA gives a stable, unbiased platform for families to ...
Families of Spinal Muscular Atrophy - Mon, 25 Aug 2014 06:18
|Mother fighting for son afflicted with SMA|
Beckley Register-Herald - Mon, 25 Aug 2014 00:04
|Families of SMA provides critical services to families recently diagnosed with ...|
Families of SMA has invested nearly $57 million in SMA research in our 30-year history. But funding research is not the whole of our mission. We also provide compassionate, respectful support for all individuals and families who are affected by SMA ...
Families of Spinal Muscular Atrophy - Thu, 14 Aug 2014 08:00
|SMA Researchers Talk About the Importance of the Spinal Muscular Atrophy ...|
The SMA research group meeting, held each year as part of our Annual SMA Conference, is an anticipated event in the SMA research community. This meeting has a tangible impact on achieving our mission of a world without SMA. Over the last decade, ...
Families of Spinal Muscular Atrophy - Tue, 12 Aug 2014 15:52
|Isis Initiates Phase 3 Clinical Trial in Infants with Spinal Muscular Atrophy.|
Isis Pharmaceuticals, Inc. announced today the initiation of a pivotal Phase 3 study evaluating ISIS-SMNRx in infants with spinal muscular atrophy (SMA). The Phase 3 study, ENDEAR, is the first of several planned studies in a broad and comprehensive ...
Families of Spinal Muscular Atrophy - Fri, 01 Aug 2014 05:00
|Isis Pharmaceuticals Initiates Phase 3 Study of ISIS-SMN Rx in Infants with ...|
PR Newswire (press release) - Fri, 01 Aug 2014 03:52
|Exciting Weekend for Families of Spinal Muscular Atrophy Fundraising Events|
Exciting Weekend for Families of Spinal Muscular Atrophy Fundraising Events. August 22, 2014. As our fall event season is now in full swing, please join our chapters as we kick off events in Indiana, Wisconsin, Colorado, North and South Carolina, New ...
Families of Spinal Muscular Atrophy - Fri, 22 Aug 2014 13:03