|SCARLET'S STORY: Stephen Clark's granddaughter braves battle against SMA ...|
In a nutshell, her body cannot build muscles, and what she has is slowly wasting away. Her mother is my daughter, Hillary Goszczynski. “Scarlet individually is pretty much affected from her armpits down… she's very floppy overall — her legs don't ...
WXYZ - Thu, 26 Mar 2015 13:03
|Research and Markets: Spinal Muscular Atrophy Pipeline Highlights 2014-2017|
The latest report Spinal Muscular Atrophy Pipeline Highlights - 2015, provides most up-to-date information on key pipeline molecules in the global Spinal Muscular Atrophy market. It covers emerging therapies for Spinal Muscular Atrophy in active ...
Yahoo Finance UK - Mon, 23 Mar 2015 09:52
|Potential New Spinal Muscular Atrophy Therapeutic Target Found in Mice|
SMA is a rare, devastating motor neuron disease and one of the leading genetic causes of pediatric mortality, occurring in approximately 1 in every 6,000 to 10,000 newborns. It is characterized by the degeneration of nerves controlling muscles and ...
SMA News Today - Thu, 19 Mar 2015 11:07
|Research and Markets: Spinal Muscular Atrophy (SMA) Therapeutics Pipeline ...|
This report provides comprehensive information on the therapeutic development for Spinal Muscular Atrophy (SMA), complete with comparative analysis at various stages, therapeutics assessment by drug target, mechanism of action (MoA), route of ...
Business Wire (press release) - Tue, 03 Mar 2015 02:30
|Harris/Hambro Family Medical Donation For Baby Tucker Diagnosed with Spinal ...|
Tucker has been diagnosed with Spinal Muscular Atrophy (SMA) Type 1. This is a genetic disease that results in symmetric muscle weakness and atrophy. Type 1 children are especially at risk because of the weakness of their lung and chest muscles.
The Roundup - Tue, 24 Mar 2015 08:32
|Isis Earns $9 Mln Milestone Payment From Biogen Idec|
related to advancing the ongoing pivotal Phase 3 study evaluating ISIS-SMN in infants with spinal muscular atrophy or SMA. ENDEAR, a Phase 3 study of ISIS-SMN, is a randomized, double-blind, sham-procedure controlled thirteen month study in about 110 ...
Nasdaq - Fri, 06 Mar 2015 04:00
|Isis Pharma (ISIS) Earns $9M Milestone in Biogen (BIIB) Collaboration|
StreetInsider.com - Fri, 06 Mar 2015 04:00
|Isis Pharmaceuticals Earns $9M for Advancing ISIS-SMN Rx in Infants With ...|
Virtual Press Office (press release) - Fri, 06 Mar 2015 04:00
|Five inventive Niskayuna women alumni make mark|
When Amy Jaffe Barzach lost her 9-month-old son to spinal muscular atrophy, she faced her grief by working to improve the world for children with disabilities. Her son would have needed a wheelchair if he had survived, but Jaffe Barzach realized most ...
Your Niskayuna (blog) - Thu, 26 Mar 2015 09:52
|Need for Pediatric Home Care|
"At four months old she was diagnosed with spinal muscular atrophy type one," said mother Shannon Hiley. At the time, Hiley realized she needed a home-care nurse, because Braylin has to be closely monitored and it isn't easy to use her medical equipment.
KAALtv.com - Thu, 26 Mar 2015 17:11